sepiapterin

FDA Drug Profile — Sephience

Drug Details

Generic Name
sepiapterin
Brand Names
Sephience
Application Number
NDA219666
Sponsor
PTC Therapeutics Inc.
NDC Codes
2
Dosage Forms
POWDER
Routes
ORAL
Active Ingredients
SEPIAPTERIN

Indications and Usage

1 INDICATIONS AND USAGE SEPHIENCE is indicated for the treatment of hyperphenylalaninemia (HPA) in adult and pediatric patients 1 month of age and older with sepiapterin-responsive phenylketonuria (PKU). SEPHIENCE is to be used in conjunction with a phenylalanine (Phe)-restricted diet. SEPHIENCE is a phenylalanine hydroxylase (PAH) activator indicated for the treatment of hyperphenylalaninemia (HPA) in adult and pediatric patients 1 month of age and older with sepiapterin-responsive phenylketonuria (PKU). SEPHIENCE is to be used in conjunction with a phenylalanine (Phe)- restricted diet. ( 1 )